{"id":53002,"date":"2025-12-19T19:48:35","date_gmt":"2025-12-19T10:48:35","guid":{"rendered":"https:\/\/www.marketresearch.jp\/reports\/?p=53002"},"modified":"2026-09-25T04:30:00","modified_gmt":"2026-09-24T19:30:00","slug":"gene-therapy-for-sickle-cell-disease-market","status":"publish","type":"post","link":"https:\/\/www.marketresearch.jp\/reports\/gene-therapy-for-sickle-cell-disease-market\/","title":{"rendered":"\u4e16\u754c\u306e\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\uff1a\u6cbb\u7642\u30e2\u30c7\u30eb\u5225\uff08\u4ed6\u5bb6\u3001\u81ea\u5df1\uff09\u3001\u6539\u5909\u6280\u8853\u5225\uff08\u5869\u57fa\u7de8\u96c6\u3001CRISPR\/Cas9\u3001\u30ec\u30f3\u30c1\u30a6\u30a4\u30eb\u30b9\u30d9\u30af\u30bf\u30fc\uff09\u3001\u60a3\u8005\u5e74\u9f62\u5225\u3001\u91cd\u75c7\u5ea6\u5225\u3001\u652f\u6255\u8005\u533a\u5206\u5225\u3001\u6d41\u901a\u30c1\u30e3\u30cd\u30eb\u5225 – \u30b0\u30ed\u30fc\u30d0\u30eb\u4e88\u6e2c 2025-2032"},"content":{"rendered":"

\"Market<\/p>\n

\u4ee5\u4e0b\u306bTOC\u306e\u65e5\u672c\u8a9e\u8a33\u3068\u8a73\u7d30\u306a\u968e\u5c64\u69cb\u9020\u3092\u793a\u3057\u307e\u3059\u3002<\/p>\n

—<\/p>\n

## \u76ee\u6b21<\/p>\n

* **\u5e8f\u6587**
\n * \u5e02\u5834\u30bb\u30b0\u30e1\u30f3\u30c6\u30fc\u30b7\u30e7\u30f3\u3068\u30ab\u30d0\u30ec\u30c3\u30b8
\n * \u8abf\u67fb\u5bfe\u8c61\u671f\u9593
\n * \u901a\u8ca8
\n * \u8a00\u8a9e
\n * \u30b9\u30c6\u30fc\u30af\u30db\u30eb\u30c0\u30fc
\n* **\u8abf\u67fb\u65b9\u6cd5\u8ad6**
\n* **\u30a8\u30b0\u30bc\u30af\u30c6\u30a3\u30d6\u30b5\u30de\u30ea\u30fc**
\n* **\u5e02\u5834\u6982\u8981**
\n* **\u5e02\u5834\u30a4\u30f3\u30b5\u30a4\u30c8**
\n * \u938c\u72b6\u8d64\u8840\u7403\u75c7\u6cbb\u7642\u306b\u304a\u3044\u3066\u9ad8\u3044\u30aa\u30f3\u30bf\u30fc\u30b2\u30c3\u30c8\u52b9\u7387\u3068\u30aa\u30d5\u30bf\u30fc\u30b2\u30c3\u30c8\u30ea\u30b9\u30af\u306e\u4f4e\u6e1b\u3092\u793a\u3059\u65b0\u305f\u306aCRISPR\u30d9\u30fc\u30b9\u7de8\u96c6\u30d7\u30e9\u30c3\u30c8\u30d5\u30a9\u30fc\u30e0
\n * \u7c73\u56fd\u306b\u304a\u3051\u308b\u938c\u72b6\u8d64\u8840\u7403\u75c7\u60a3\u8005\u5411\u3051\u30d5\u30a1\u30fc\u30b9\u30c8\u30a4\u30f3\u30af\u30e9\u30b9\u907a\u4f1d\u5b50\u6cbb\u7642\u3092\u5f62\u6210\u3059\u308b\u898f\u5236\u7d4c\u8def\u3068\u8fc5\u901f\u627f\u8a8d\u30d7\u30ed\u30b0\u30e9\u30e0
\n * \u5e0c\u5c11\u8840\u6db2\u75be\u60a3\u306b\u304a\u3051\u308b\u5546\u696d\u7528\u907a\u4f1d\u5b50\u6cbb\u7642\u306e\u5e02\u5834\u30a2\u30af\u30bb\u30b9\u306b\u5f71\u97ff\u3092\u4e0e\u3048\u308b\u8cbb\u7528\u5bfe\u52b9\u679c\u30e2\u30c7\u30eb\u3068\u652f\u6255\u8005\u4ea4\u6e09
\n * \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u53d7\u7d66\u8005\u306e\u5e02\u8ca9\u5f8c\u76e3\u8996\u306e\u305f\u3081\u306e\u9577\u671f\u5b89\u5168\u6027\u30e2\u30cb\u30bf\u30ea\u30f3\u30b0\u3068\u30ea\u30a2\u30eb\u30ef\u30fc\u30eb\u30c9\u30a8\u30d3\u30c7\u30f3\u30b9\u751f\u6210
\n * \u907a\u4f1d\u5b50\u6cbb\u7642\u306b\u304a\u3051\u308b\u81ea\u5bb6\u7d30\u80de\u51e6\u7406\u306e\u305f\u3081\u306e\u81ea\u52d5\u30d0\u30a4\u30aa\u30ea\u30a2\u30af\u30bf\u30fc\u3092\u7528\u3044\u305f\u30b5\u30d7\u30e9\u30a4\u30c1\u30a7\u30fc\u30f3\u6700\u9069\u5316\u3068\u88fd\u9020\u30b9\u30b1\u30fc\u30e9\u30d3\u30ea\u30c6\u30a3
\n * \u938c\u72b6\u8d64\u8840\u7403\u75c7\u6cbb\u7642\u306e\u81e8\u5e8a\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u306b\u304a\u3051\u308b\u30ec\u30f3\u30c1\u30a6\u30a4\u30eb\u30b9\u30d9\u30fc\u30b9\u3068CRISPR\u30d9\u30fc\u30b9\u306e\u30a2\u30d7\u30ed\u30fc\u30c1\u306e\u7af6\u5408\u60c5\u52e2\u5206\u6790
\n * \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u8a66\u9a13\u306b\u304a\u3051\u308b\u4fa1\u5024\u63d0\u6848\u3092\u63a8\u9032\u3059\u308b\u60a3\u8005\u4e2d\u5fc3\u306e\u30a2\u30a6\u30c8\u30ab\u30e0\u6307\u6a19\u3068QOL\u8a55\u4fa1
\n* **2025\u5e74\u7c73\u56fd\u95a2\u7a0e\u306e\u7d2f\u7a4d\u7684\u5f71\u97ff**
\n* **2025\u5e74\u4eba\u5de5\u77e5\u80fd\u306e\u7d2f\u7a4d\u7684\u5f71\u97ff**
\n* **\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u3001\u6cbb\u7642\u30e2\u30c7\u30eb\u5225**
\n * \u540c\u7a2e
\n * \u81ea\u5bb6
\n* **\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u3001\u6539\u5909\u6280\u8853\u5225**
\n * \u30d9\u30fc\u30b9\u7de8\u96c6
\n * CRISPR\/Cas9
\n * \u30ec\u30f3\u30c1\u30a6\u30a4\u30eb\u30b9\u30d9\u30af\u30bf\u30fc
\n * \u30b8\u30f3\u30af\u30d5\u30a3\u30f3\u30ac\u30fc\u30cc\u30af\u30ec\u30a2\u30fc\u30bc
\n* **\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u3001\u60a3\u8005\u5e74\u9f62\u5225**
\n * \u6210\u4eba
\n * \u5c0f\u5150
\n* **\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u3001\u91cd\u75c7\u5ea6\u5225**
\n * \u4e2d\u7a0b\u5ea6
\n * \u91cd\u5ea6
\n* **\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u3001\u652f\u6255\u8005\u30ab\u30c6\u30b4\u30ea\u5225**
\n * \u653f\u5e9c
\n * \u81ea\u5df1\u8ca0\u62c5
\n * \u6c11\u9593
\n* **\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u3001\u6d41\u901a\u30c1\u30e3\u30cd\u30eb\u5225**
\n * \u75c5\u9662
\n * \u5c02\u9580\u6cbb\u7642\u30bb\u30f3\u30bf\u30fc
\n* **\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u3001\u5730\u57df\u5225**
\n * \u7c73\u5dde
\n * \u5317\u7c73
\n * \u4e2d\u5357\u7c73
\n * \u6b27\u5dde\u3001\u4e2d\u6771\u3001\u30a2\u30d5\u30ea\u30ab
\n * \u6b27\u5dde
\n * \u4e2d\u6771
\n * \u30a2\u30d5\u30ea\u30ab
\n * \u30a2\u30b8\u30a2\u592a\u5e73\u6d0b
\n* **\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u3001\u30b0\u30eb\u30fc\u30d7\u5225**
\n * ASEAN
\n * GCC
\n * \u6b27\u5dde\u9023\u5408
\n * BRICS
\n * G7
\n * NATO
\n* **\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u3001\u56fd\u5225**
\n * \u7c73\u56fd
\n * \u30ab\u30ca\u30c0
\n * \u30e1\u30ad\u30b7\u30b3
\n * \u30d6\u30e9\u30b8\u30eb
\n * \u82f1\u56fd
\n * \u30c9\u30a4\u30c4
\n * \u30d5\u30e9\u30f3\u30b9
\n * \u30ed\u30b7\u30a2
\n * \u30a4\u30bf\u30ea\u30a2
\n * \u30b9\u30da\u30a4\u30f3
\n * \u4e2d\u56fd
\n * \u30a4\u30f3\u30c9
\n * \u65e5\u672c
\n * \u30aa\u30fc\u30b9\u30c8\u30e9\u30ea\u30a2
\n * \u97d3\u56fd
\n* **\u7af6\u5408\u60c5\u52e2**
\n * \u5e02\u5834\u30b7\u30a7\u30a2\u5206\u6790\u30012024\u5e74
\n * FPNV\u30dd\u30b8\u30b7\u30e7\u30cb\u30f3\u30b0\u30de\u30c8\u30ea\u30c3\u30af\u30b9\u30012024\u5e74
\n * \u7af6\u5408\u5206\u6790
\n * Bluebird Bio, Inc.
\n * CRISPR Therapeutics AG
\n * Vertex Pharmaceuticals Incorporated
\n * Sangamo Therapeutics, Inc.
\n * Editas Medicine, Inc.
\n * Beam Therapeutics, Inc.
\n * Graphite Bio, Inc.
\n * Homology Medicines, Inc.
\n * Intellia Therapeutics, Inc.
\n * Precision BioSciences, Inc.
\n* **\u56f3\u76ee\u6b21 [\u5408\u8a08: 32]**
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u30012018-2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u6cbb\u7642\u30e2\u30c7\u30eb\u5225\u30012024\u5e74\u5bfe2032\u5e74\uff08%\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u6cbb\u7642\u30e2\u30c7\u30eb\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u6539\u5909\u6280\u8853\u5225\u30012024\u5e74\u5bfe2032\u5e74\uff08%\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u6539\u5909\u6280\u8853\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u60a3\u8005\u5e74\u9f62\u5225\u30012024\u5e74\u5bfe2032\u5e74\uff08%\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u60a3\u8005\u5e74\u9f62\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u91cd\u75c7\u5ea6\u5225\u30012024\u5e74\u5bfe2032\u5e74\uff08%\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u91cd\u75c7\u5ea6\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u652f\u6255\u8005\u30ab\u30c6\u30b4\u30ea\u5225\u30012024\u5e74\u5bfe2032\u5e74\uff08%\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u652f\u6255\u8005\u30ab\u30c6\u30b4\u30ea\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u6d41\u901a\u30c1\u30e3\u30cd\u30eb\u5225\u30012024\u5e74\u5bfe2032\u5e74\uff08%\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u6d41\u901a\u30c1\u30e3\u30cd\u30eb\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u5730\u57df\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * \u7c73\u5dde \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u30b5\u30d6\u5730\u57df\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * \u5317\u7c73 \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u56fd\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * \u4e2d\u5357\u7c73 \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u56fd\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * \u6b27\u5dde\u3001\u4e2d\u6771\u3001\u30a2\u30d5\u30ea\u30ab \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u30b5\u30d6\u5730\u57df\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * \u6b27\u5dde \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u56fd\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * \u4e2d\u6771 \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u56fd\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * \u30a2\u30d5\u30ea\u30ab \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u56fd\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * \u30a2\u30b8\u30a2\u592a\u5e73\u6d0b \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u56fd\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * GLOBAL \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u30b0\u30eb\u30fc\u30d7\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * ASEAN \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u56fd\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * GCC \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u898f\u6a21\u3001\u56fd\u5225\u30012024\u5e74\u5bfe2025\u5e74\u5bfe2032\u5e74\uff08\u767e\u4e07\u7c73\u30c9\u30eb\uff09
\n * \u6b27\u5dde\u9023\u5408 \u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642<\/p>\n

………… (\u4ee5\u4e0b\u7701\u7565)<\/p>\n","protected":false},"excerpt":{"rendered":"

\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u306f\u30012025\u5e74\u304b\u30892032\u5e74\u306b\u304b\u3051\u3066\u3001\u3053\u306e\u907a\u4f1d\u6027\u8840\u6db2\u75be\u60a3\u306e\u6cbb\u7642\u30d1\u30e9\u30c0\u30a4\u30e0\u3092\u6839\u672c\u7684\u306b\u5909\u9769\u3059\u308b\u53ef\u80fd\u6027\u3092\u79d8\u3081\u3066\u3044\u307e\u3059\u3002\u938c\u72b6\u8d64\u8840\u7403\u75c7\u306f\u3001\u7570\u5e38\u306a\u5f62\u72b6\u306e\u8d64\u8840\u7403\u304c\u5fae\u5c0f\u8840\u7ba1\u3092\u9589\u585e\u3055\u305b\u3001\u6162\u6027\u6eb6\u8840\u3001\u6025\u6027\u75bc\u75db\u767a\u4f5c\u3001\u8133\u5352\u4e2d\u3001\u814e\u6a5f\u80fd\u969c\u5bb3\u3001\u80ba\u9ad8\u8840\u5727\u75c7\u3068\u3044\u3063\u305f\u591a\u81d3\u5668\u5408\u4f75\u75c7\u3092\u5f15\u304d\u8d77\u3053\u3059\u907a\u4f1d\u6027\u8840\u6db2\u75be\u60a3\u3067\u3059\u3002\u7c73\u56fd\u3060\u3051\u3067\u3082\u7d0410\u4e07\u4eba\u304c\u3053\u306e\u75be\u60a3\u3092\u62b1\u3048\u3001\u4e16\u754c\u7684\u306b\u306f\u30b5\u30cf\u30e9\u4ee5\u5357\u30a2\u30d5\u30ea\u30ab\u3001\u30a4\u30f3\u30c9\u3001\u4e2d\u6771\u306e\u4e00\u90e8\u3067\u6570\u767e\u4e07\u4eba\u304c\u5f71\u97ff\u3092\u53d7\u3051\u3066\u304a\u308a\u3001\u751f\u6daf\u306b\u308f\u305f\u308b\u7f79\u60a3\u3068\u65e9\u671f\u6b7b\u4ea1\u306e\u30ea\u30b9\u30af\u306b\u76f4\u9762\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n

\u5f93\u6765\u306e\u6cbb\u7642\u6cd5\u306f\u4e3b\u306b\u652f\u6301\u7642\u6cd5\u3067\u3042\u308a\u3001FDA\u627f\u8a8d\u85ac\u3067\u3042\u308b\u30d2\u30c9\u30ed\u30ad\u30b7\u5c3f\u7d20\u306f\u80ce\u5150\u30d8\u30e2\u30b0\u30ed\u30d3\u30f3\u7523\u751f\u3092\u8a98\u5c0e\u3057\u3001\u8840\u7ba1\u9589\u585e\u30a4\u30d9\u30f3\u30c8\u3092\u6e1b\u5c11\u3055\u305b\u308b\u7b2c\u4e00\u9078\u629e\u85ac\u3067\u3059\u304c\u3001\u591a\u304f\u306e\u60a3\u8005\u306f\u6700\u9069\u306a\u6295\u4e0e\u91cf\u3068\u9075\u5b88\u306b\u3082\u304b\u304b\u308f\u3089\u305a\u3001\u4f9d\u7136\u3068\u3057\u3066\u8870\u5f31\u6027\u306e\u75c7\u72b6\u3092\u7d4c\u9a13\u3057\u3066\u3044\u307e\u3059\u3002\u8f38\u8840\u7642\u6cd5\u3084\u9244\u30ad\u30ec\u30fc\u30c8\u7642\u6cd5\u3082\u5408\u4f75\u75c7\u3092\u8efd\u6e1b\u3057\u307e\u3059\u304c\u3001\u9244\u904e\u5270\u75c7\u3084\u540c\u7a2e\u514d\u75ab\u306a\u3069\u306e\u9577\u671f\u7684\u306a\u30ea\u30b9\u30af\u3092\u4f34\u3044\u307e\u3059\u3002\u3053\u308c\u3089\u306e\u6cbb\u7642\u6cd5\u306f\u75be\u60a3\u7ba1\u7406\u306e\u57fa\u76e4\u3092\u5f62\u6210\u3057\u307e\u3059\u304c\u3001\u4e00\u6642\u7684\u306a\u6709\u52b9\u6027\u3068\u7d2f\u7a4d\u6bd2\u6027\u306b\u3088\u3063\u3066\u5236\u7d04\u3055\u308c\u307e\u3059\u3002\u540c\u7a2e\u9020\u8840\u5e79\u7d30\u80de\u79fb\u690d\u306f\u3001\u6b20\u9665\u306e\u3042\u308b\u9aa8\u9ac4\u3092\u9069\u5408\u30c9\u30ca\u30fc\u306e\u7d30\u80de\u306b\u7f6e\u304d\u63db\u3048\u308b\u3053\u3068\u3067\u6f5c\u5728\u7684\u306a\u6cbb\u7652\u6cd5\u3092\u63d0\u4f9b\u3057\u307e\u3059\u304c\u3001\u30c9\u30ca\u30fc\u306e\u5229\u7528\u53ef\u80fd\u6027\u3001\u79fb\u690d\u7247\u5bfe\u5bbf\u4e3b\u75c5\u306e\u30ea\u30b9\u30af\u3001\u7279\u306b\u81d3\u5668\u640d\u50b7\u306e\u3042\u308b\u6210\u4eba\u60a3\u8005\u306b\u304a\u3051\u308b\u6cbb\u7642\u95a2\u9023\u6b7b\u4ea1\u7387\u306b\u3088\u3063\u3066\u305d\u306e\u9069\u7528\u306f\u9650\u3089\u308c\u3066\u3044\u307e\u3059\u3002\u3055\u3089\u306b\u3001\u79fb\u690d\u524d\u51e6\u7f6e\u30ec\u30b8\u30e1\u30f3\u306f\u8ffd\u52a0\u306e\u5b89\u5168\u4e0a\u306e\u61f8\u5ff5\u3092\u5f15\u304d\u8d77\u3053\u3057\u3001\u901a\u5e38\u306f\u9069\u5207\u306a\u30c9\u30ca\u30fc\u3092\u6301\u3064\u5c0f\u5150\u60a3\u8005\u306b\u9650\u5b9a\u3055\u308c\u307e\u3059\u3002\u305d\u306e\u7d50\u679c\u3001\u5927\u591a\u6570\u306e\u60a3\u8005\u306f\u6c7a\u5b9a\u7684\u306a\u6839\u6cbb\u7684\u9078\u629e\u80a2\u306b\u30a2\u30af\u30bb\u30b9\u3067\u304d\u305a\u3001\u3053\u308c\u3089\u306e\u6e80\u305f\u3055\u308c\u306a\u3044\u533b\u7642\u30cb\u30fc\u30ba\u304c\u9769\u65b0\u7684\u306a\u6cbb\u7642\u30a2\u30d7\u30ed\u30fc\u30c1\u306e\u7dca\u6025\u6027\u3092\u5f37\u8abf\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n

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\u938c\u72b6\u8d64\u8840\u7403\u75c7\u907a\u4f1d\u5b50\u6cbb\u7642\u5e02\u5834\u3092\u727d\u5f15\u3059\u308b\u8981\u56e0\u306f\u591a\u5c90\u306b\u308f\u305f\u308a\u307e\u3059\u3002\u6700\u3082\u5148\u9032\u7684\u306a\u958b\u767a\u30d7\u30ed\u30b0\u30e9\u30e0\u306f\u3001\u75be\u60a3\u306e\u57fa\u790e\u75c5\u614b\u306b\u5bfe\u51e6\u3059\u308b\u305f\u3081\u306b\u591a\u69d8\u306a\u907a\u4f1d\u5b50\u6539\u5909\u30d7\u30e9\u30c3\u30c8\u30d5\u30a9\u30fc\u30e0\u3092\u6d3b\u7528\u3057\u3066\u3044\u307e\u3059\u3002CRISPR\/Cas9\u30d9\u30fc\u30b9\u306e\u6cbb\u7642\u6cd5\uff08CTX001\u306a\u3069\uff09\u306f\u3001\u6a19\u7684\u3068\u306a\u308b\u4e8c\u672c\u9396\u5207\u65ad\u3092\u5229\u7528\u3057\u3066\u80ce\u5150\u30d8\u30e2\u30b0\u30ed\u30d3\u30f3\u3092\u4e0a\u65b9\u5236\u5fa1\u3057\u307e\u3059\u3002BEAM-101\u306e\u3088\u3046\u306a\u30d9\u30fc\u30b9\u7de8\u96c6\u30a2\u30d7\u30ed\u30fc\u30c1\u306f\u3001\u5e83\u7bc4\u306a\u30b2\u30ce\u30e0\u7834\u58ca\u3092\u5f15\u304d\u8d77\u3053\u3059\u3053\u3068\u306a\u304f\u6b63\u78ba\u306a\u30cc\u30af\u30ec\u30aa\u30c1\u30c9\u5909\u5316\u3092\u5c0e\u5165\u3057\u307e\u3059\u3002\u30ec\u30f3\u30c1\u30a6\u30a4\u30eb\u30b9\u30d9\u30af\u30bf\u30fc\u3092\u4ecb\u3057\u305f\u907a\u4f1d\u5b50\u5c0e\u5165\u306f\u3001\u6297\u938c\u72b6\u5316\u30b0\u30ed\u30d3\u30f3\u5909\u7570\u4f53\u306e\u6301\u7d9a\u7684\u306a\u767a\u73fe\u3092\u5b9f\u73fe\u3057\u3001\u30b8\u30f3\u30af\u30d5\u30a3\u30f3\u30ac\u30fc\u30cc\u30af\u30ec\u30a2\u30fc\u30bc\u306fin vivo\u7de8\u96c6\u306e\u6982\u5ff5\u5b9f\u8a3c\u3092\u793a\u3057\u3066\u3044\u307e\u3059\u3002\u5404\u30e2\u30c0\u30ea\u30c6\u30a3\u306f\u7570\u306a\u308b\u7de8\u96c6\u52b9\u7387\u3001\u30aa\u30d5\u30bf\u30fc\u30b2\u30c3\u30c8\u30ea\u30b9\u30af\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\u3001\u898f\u5236\u4e0a\u306e\u8907\u96d1\u3055\u3092\u4f34\u3044\u307e\u3059\u304c\u3001\u3059\u3079\u3066\u304c\u4e00\u56de\u9650\u308a\u306e\u6f5c\u5728\u7684\u306b\u6839\u6cbb\u7684\u306a\u6cbb\u7642\u3068\u3044\u3046\u7d04\u675f\u3092\u5171\u6709\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n

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